Four decades of Orphan Drug Act momentum amplifies the need for broader access to treatment of rare diseases, say NORD’s Karin Hoelzer and Fondation Ipsen’s James Levine.

As the first sickle cell patient treated with CRISPR, Victoria Gray moved from agonizing pain toward an astonishing cure. Ghanaian journalist Portia Gabor relishes telling stories like hers.

Journalists should help explain ‘the why’ behind the problems within caregiving, says The Wall Street Journal’s Clare Ansberry.

Aging is a priority for the National Academy for State Health Policy, says Hemi Tewarson.

Black adults see inequity as they age due to the systemic history of racism, says Karyne Jones.

There are national systemic consequences within long-term care, Washington Post reporter Christopher Rowland says.

There’s a lack of options in long-term care and services, yet ‘choice is key,’ says Rita Choula of AARP and Joon Bang of Iona Senior Services.

Unpaid family caregivers outnumber paid long-term workers tenfold, leading many to ask: Who's caring for the caregivers?

Veteran NPR Producer Kitty Eisele could not prepare for the toll that caring for her father Al would take. Her podcast gives voice to the struggles that families face.

Family caregivers face dire economic and health consequences from caring for loved ones, but many also find a sense of purpose or fulfillment, says Jason Resendez of National Alliance for Caregiving.

Lauren Miller Rogen and James Keach hope their upcoming documentary will inspire and motivate millions of families coping with Alzheimer’s.

Washington Post’s Michelle Singletary and SCAN Foundation President Sarita Mohanty urge journalists to demystify caregiving costs.

MSNBC’s Richard Lui and Alex Lo of NBC were caregivers for their own family members. Then, they made films about caregivers across the country.

Americans need more support, say Debra Whitman and Susan Reinhard of AARP.

Dr. Sandeep Jauhar wrote “My Father’s Brain” about his family’s experience with Alzheimer's – including his own struggles as a caregiver.

For updated COVID vaccine access, pharmacies will be where the “friction” is in the weeks ahead, doctor says.

Edward Barksdale knows how to mend a wounded heart. But the Surgeon-in-Chief at Rainbow Babies and Children’s Hospital also vows to heal traumatized communities.

Childhood obesity can be treated, but the social determinants of health hold more sway than surgery or nixing sugary soda, says the Cleveland Clinic’s Dr. Roy Kim.

Undocumented parents often don’t seek health care for fear of deportation. Journalists can help kids stay covered, experts from the Children’s Defense Fund Texas said.

Toxic bosses, burnout, turnover and unionization prompt new emphasis on workplace well-being.

The WTO compromise on a Trade-Related Aspects of Intellectual Property Rights (TRIPS) waiver has not settled the debate.

While TikTok videos about epigenetics and trauma rack up millions of likes, the science continues to evolve.

Tips for reporters covering the coronavirus vaccine for children — and how it will impact families, schools and more.

But journalists should also focus on regulation of the AI and electronic medical records that underlie biotech gains.

In the U.S., the Orphan Drug Act incentivizes drugmakers to develop drugs for rare disease patients, including 31 in 2020.

From Ghana to Australia, rare disease researchers and patient groups prod their governments to action — and international cooperation.

Nearly 8% of the world’s population — 350 million people — have a rare disease. But diagnosis and treatment are advancing.

Nearly 8% of the world’s population — 350 million people — have a rare disease. But diagnosis and treatment are advancing.

As the FDA allows more big data for drug and device approvals, top researchers share studies that show its potential — and flaws. One drug-safety expert warns against abandoning the randomized controlled trial.

Some experts call for U.S. digital credential to prove vaccine status, but others warn it could increase inequality and discrimination.

Randomized clinical trials have long been the gold standard for drug and device approvals. Now Big Data powers “real-world evidence” that plays a growing role in medical decisions and FDA approvals.

Google and public health officials have developed tools reporters can use to pinpoint “vaccine deserts” and communities where people are searching about vaccine side effects.

Three new types of addiction-treatment drugs show promise, as researchers apply understanding of cancer, Alzheimer’s disease, epigenetics and anxiety to developing medicines that can lessen cravings and relapses.

Opioids changed the geography and politics of America’s addition problem. Here’s how three writers made readers care about the story.

Immigrant Latinos are healthier, physically and mentally, when they arrive in the U.S. than later, research finds A dearth of Latino health-care professionals hurts.

Physicians won’t be replaced by iPhones, but “a therapist in your pocket” can help improve treatment for substance use disorders.

Experts decry systemic racism in the treatment of opioid addiction. More Black patients have to line up to get methadone. White Americans are more likely to get buprenorphine prescribed from the privacy of a doctor’s office.

A family history of alcohol use disorder is the most important risk factor. A top addiction doctor details the latest research.

Just when the U.S. began winning the war on prescription opioid misuse, synthetic fentanyl smuggled from China and Mexico has created an “unprecedented” increase in overdose deaths.

Addiction specialist Dr. Stephen Taylor has been calling for sweeping reforms in the racialized treatment of substance use disorders. He calls on physicians and law enforcement to rethink a chronic, relapsing brain disorder.